Medicinefromwww.nature.com3 days agoGene Therapy Marks a Turning Point for Rare Skin DiseasesTopical gene therapy B-VEC healed chronic wounds and restored mobility and independence for children with epidermolysis bullosa.
MedicinefromNature1 week agoGene therapy marks a turning point for rare skin diseasesTopical gene therapy B-VEC now enables healing of chronic wounds in epidermolysis bullosa patients, transforming mobility, independence, and paving the way for graft-based treatments.
Fashion & stylefromThe New Yorker3 weeks agoThe Disease that Accelerates Aging in KidsProgeria could potentially be cured through new gene-editing treatments.
WomenfromIndependent2 months ago'I basically lost my speech language skills. I didn't know how to communicate' - Dublin star Niamh Crowley on recovery from rare diseaseNiamh Crowley transitioned from overcoming a rare disease to achieving sports success and academic pursuits.