Argentinian couple moves to US to allow their toddler to join gene therapy trialParents refused to give up despite rare disease diagnosis, traveled for gene therapy trial, showing hope and perseverance.
Luxembourg's Prince Frederik dies of rare disease DW 03/10/2025Prince Frederik of Luxembourg died at 22 from POLG mitochondrial disease, a condition with no known treatment that causes multiple organ failure.
Argentinian couple moves to US to allow their toddler to join gene therapy trialParents refused to give up despite rare disease diagnosis, traveled for gene therapy trial, showing hope and perseverance.
Luxembourg's Prince Frederik dies of rare disease DW 03/10/2025Prince Frederik of Luxembourg died at 22 from POLG mitochondrial disease, a condition with no known treatment that causes multiple organ failure.
Sammy Basso, Advocate for Progeria Research, Is Dead at 28Sammy Basso was a progeria advocate who lived humorously and courageously, raising awareness and contributing to research until his death at age 28.
When our young son died, we decided to build him a boatThe story highlights the impact of a rare disease on a child's life and the power of imagination and adventure in coping with challenges.