OMG sciencefromwww.npr.org1 week agoA promising genetic treatment tailor-made for a baby born with a rare disorderDoctors have successfully treated a baby with a rare genetic disorder using bespoke gene-editing therapy, showing promising early results.
Parentingfromwww.standard.co.uk2 months agoGene therapy experiment gives children 'life-changing' sight boost at London hospitalPioneering gene therapy restores sight in young children with a rare genetic condition.