"A chubby-cheekedbaby called KJ made medical history last year. Faced with a life-threatening metabolic disease, KJ's doctors at Children's Hospital of Philadelphia sprinted to create a personalized therapy aimed at fixing the genetic typo at the root of his illness. Like a team of superheroes assembling, they called in the best in the field to help save a baby's life."
"Among them was David Liu, a biochemist at the Broad Institute and Harvard University in Cambridge, Massachusetts. Liu isn't a medical doctor. But for a decade, he's been at the forefront of a revolution in medicine, inventing powerful and precise tools to edit the code of life. A person's DNA is a 3 billion letter tome. Misspellings, typos and omissions in the text cause thousands of illnesses."
A baby named KJ received a personalized therapy to fix a life-threatening metabolic mutation and went home after 307 days in the hospital. David Liu, a biochemist at the Broad Institute and Harvard University, developed base editing in 2016 to change single DNA bases and designed the base editor used to correct KJ's mutation. Liu also created prime editing and a method to make one edit that could address multiple rare diseases in a single therapy. He has co-founded several gene-editing companies and is raising funds for a nonprofit center to expand treatments.
Read at The Washington Post
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