fromwww.theguardian.com
3 days agoGroundbreaking UK gene therapy offers hope after progress of three-year-old
Things look really hopeful right now, but Ollie was the first human to receive this therapy and it's only been nine months out, said Prof Simon Jones, consultant in paediatric inherited metabolic disease at the Manchester Centre for Genomic Medicine (MCGM) at Saint Mary's hospital. We have four more boys scheduled in and we will need to prove the benefit is long lasting, said Jones, the joint leader of the trial.
Medicine

