Medicinefromwww.nature.com2 months agoGene Editing Helped One BabyCould It Help Thousands?Personalized base-editing therapy cured baby KJ; a clinical trial plans to deliver multiple similarly tailored treatments faster after negotiating simplified regulatory pathways.
SciencefromNature2 months agoDaily briefing: Custom-made gene-editing therapy for children to enter clinical trialPersonalized CRISPR base-editing therapy that rescued an infant will enter a clinical trial for at least five more children.
