Weese-Mayer Honored with 2025 Stern Award - News CenterDebra E. Weese-Mayer, MD, receives the 2025 Paula H. Stern Award for her pioneering work in pediatric autonomic medicine.
A life in the ICU: Little Fabio's race against time as he awaited a transplantFabio's fight for lung health showcases the critical role of organ transplantation in pediatric care.His experience emphasizes the emotional and logistical challenges faced by families in medical crises.
First Day of a New Life' for a Boy With Sickle CellKendric Cromer starts a hopeful journey free from sickle cell disease thanks to new gene therapy.
Strimvelis, the gene therapy rejected by the pharmaceutical industry that has saved AitanaGene therapy saved Aitana's life after she was diagnosed with a severe immune deficiency.The Strimvelis treatment faced discontinuation, emphasizing the challenge of sustaining innovative medical therapies.
More children gain hearing as gene therapy for profound deafness advancesGene therapy is offering children with genetic deafness the ability to hear normally without the need for hearing aids or cochlear implants.
First Day of a New Life' for a Boy With Sickle CellKendric Cromer starts a hopeful journey free from sickle cell disease thanks to new gene therapy.
Strimvelis, the gene therapy rejected by the pharmaceutical industry that has saved AitanaGene therapy saved Aitana's life after she was diagnosed with a severe immune deficiency.The Strimvelis treatment faced discontinuation, emphasizing the challenge of sustaining innovative medical therapies.
More children gain hearing as gene therapy for profound deafness advancesGene therapy is offering children with genetic deafness the ability to hear normally without the need for hearing aids or cochlear implants.
New research explores the urea cycle's strong connection to fatty liver diseaseThe urea cycle plays a critical role in the development of fatty liver disease, offering potential for new treatments.
Mildred Thornton Stahlman, Pioneer in Neonatal Care, Dies at 101Dr. Mildred Thornton Stahlman pioneered lifesaving treatments for newborns with respiratory lung disease, leading to the establishment of one of the first neonatal intensive care units.