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First Day of a New Life' for a Boy With Sickle Cell

Kendric Cromer starts a hopeful journey free from sickle cell disease thanks to new gene therapy.

Strimvelis, the gene therapy rejected by the pharmaceutical industry that has saved Aitana

Gene therapy saved Aitana's life after she was diagnosed with a severe immune deficiency.
The Strimvelis treatment faced discontinuation, emphasizing the challenge of sustaining innovative medical therapies.

More children gain hearing as gene therapy for profound deafness advances

Gene therapy is offering children with genetic deafness the ability to hear normally without the need for hearing aids or cochlear implants.

First Day of a New Life' for a Boy With Sickle Cell

Kendric Cromer starts a hopeful journey free from sickle cell disease thanks to new gene therapy.

Strimvelis, the gene therapy rejected by the pharmaceutical industry that has saved Aitana

Gene therapy saved Aitana's life after she was diagnosed with a severe immune deficiency.
The Strimvelis treatment faced discontinuation, emphasizing the challenge of sustaining innovative medical therapies.

More children gain hearing as gene therapy for profound deafness advances

Gene therapy is offering children with genetic deafness the ability to hear normally without the need for hearing aids or cochlear implants.
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New research explores the urea cycle's strong connection to fatty liver disease

The urea cycle plays a critical role in the development of fatty liver disease, offering potential for new treatments.

Mildred Thornton Stahlman, Pioneer in Neonatal Care, Dies at 101

Dr. Mildred Thornton Stahlman pioneered lifesaving treatments for newborns with respiratory lung disease, leading to the establishment of one of the first neonatal intensive care units.
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