#beta-thalassemia

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Maimonides' holiday party brings comfort and cheer to pediatric patients * Brooklyn Paper

Maimonides Medical Center's holiday party enables pediatric patients to experience joy and normalcy, emphasizing the importance of mental well-being during treatment.
#sickle-cell-disease

The First Crispr Treatment Is Making Its Way to Patients

The first CRISPR-based treatment, Casgevy, has been approved for sickle cell disease and beta thalassemia, marking a significant advance in gene-editing therapies.

Gene Therapies Could Transform Treatment of Rare Blood Disorders - News Center

Gene therapy shows promising results in treating rare genetic blood disorders like beta thalassemia and sickle cell disease.

The First Crispr Treatment Is Making Its Way to Patients

The first CRISPR-based treatment, Casgevy, has been approved for sickle cell disease and beta thalassemia, marking a significant advance in gene-editing therapies.

Gene Therapies Could Transform Treatment of Rare Blood Disorders - News Center

Gene therapy shows promising results in treating rare genetic blood disorders like beta thalassemia and sickle cell disease.
moresickle-cell-disease

Vertex's CRISPR Gene Therapy Lands Another FDA Nod in a Rare Blood Disease

Vertex Pharmaceuticals and CRISPR Therapeutics' gene therapy, Casgevy, has received FDA approval as a treatment for beta thalassemia.
The therapy provides a one-time treatment option for transfusion-dependent beta thalassemia patients age 12 and older.
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