""I've been waiting 20 years to see a boy like Ollie doing as well as he is, and it's just so exciting.""
""Every time we talk about it I want to cry because it's just so amazing,""
Oliver Chu, a three-year-old with severe Hunter syndrome (MPS II), received the first-ever gene therapy aimed at correcting the faulty gene that prevents production of a crucial enzyme. The treatment involved altering Oliver's cells at Royal Manchester Children's Hospital and makes him the first of five boys worldwide to undergo this approach. One year after treatment, Oliver shows marked clinical improvement and appears to be developing normally. His family traveled from California, his older brother Skyler also has the condition, and clinicians report renewed optimism despite earlier funding challenges for the trial.
Read at www.bbc.com
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