Austin Louis is the first patient at Children's Hospital of Philadelphia, outside a clinical trial to get a newly FDA-approved gene therapy that could change his life.
Dr. Tim Olson described the gene therapy as "groundbreaking" and one of the biggest breakthroughs in the care of sickle cell disease.
The therapy involves collecting Austin Louis' stem cells and manipulating the DNA to normalize the blood, effectively preventing the sickling complications.
Jennifer Louis expressed her heartbreak over her son's condition, stating "It breaks my heart. I feel like I'm helpless, there is nothing I can do."
#sickle-cell-disease #gene-therapy #childrens-hospital-of-philadelphia #medical-breakthrough #patient-care
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