FDA has approved the first genetic treatments for sickle cell disease, offering new hope to patients like Olaide Adekanbi.
Scientists grow human brains in space to treat Alzheimer's
Microgravity facilitates rapid growth of brain organoids, enabling critical research into treatments for Alzheimer's, Parkinson's, and spinal injuries.
Gene therapy trial restores hearing in both ears for deaf children
Gene therapy trial restores hearing in deaf children, showing promise for future treatments.
First Sickle Cell Gene Therapy Patient, 12, Leaves Hospital
Kendric Cromer received the first gene therapy for sickle cell disease, representing a significant breakthrough in treatment.
The immune system can sabotage gene therapies - can scientists rein it in?
Gene therapy advancements face challenges in re-dosing after initial treatment.
Gene therapy trials treat inherited blindness and deafness DW 05/09/2024
The article highlights the groundbreaking achievement of restoring hearing and vision through gene therapy in children with rare genetic mutations.
Sickle cell gene therapies roll out slowly
FDA has approved the first genetic treatments for sickle cell disease, offering new hope to patients like Olaide Adekanbi.
Scientists grow human brains in space to treat Alzheimer's
Microgravity facilitates rapid growth of brain organoids, enabling critical research into treatments for Alzheimer's, Parkinson's, and spinal injuries.
Gene therapy trial restores hearing in both ears for deaf children
Gene therapy trial restores hearing in deaf children, showing promise for future treatments.
First Sickle Cell Gene Therapy Patient, 12, Leaves Hospital
Kendric Cromer received the first gene therapy for sickle cell disease, representing a significant breakthrough in treatment.
The immune system can sabotage gene therapies - can scientists rein it in?
Gene therapy advancements face challenges in re-dosing after initial treatment.
Gene therapy trials treat inherited blindness and deafness DW 05/09/2024
The article highlights the groundbreaking achievement of restoring hearing and vision through gene therapy in children with rare genetic mutations.
In a World First, a Patient's Antibody Cells Were Just Genetically Engineered
Seattle-based biotech company, Immusoft, has genetically programmed a patient's B cells to treat a genetic disorder known as mucopolysaccharidosis type I (MPS I).
The patient's B cells are engineered to produce an essential enzyme that his body doesn't produce, eliminating the need for regular infusions of the enzyme.
New sickle cell treatment has roots at Children's Hospital of Philadelphia
The FDA has approved the first gene therapy treatments for sickle cell disease, a blood disorder that primarily affects people of color.
The gene therapy was tested at Children's Hospital of Philadelphia and has shown promising results in patients.
'It's Transformed My Life': FDA Approves First Gene-Editing Treatment for Illness | KQED
The CRISPR treatment for sickle cell disease involves editing a gene with CRISPR and infusing the modified cells back into patients.
The therapy, Casgevy, is designed to be a one-time treatment that alleviates symptoms for a lifetime.
The U.S. FDA has approved the first gene therapy treatment based on CRISPR technology.
The treatment, called exa-cel, is approved for sickle cell disease and may also be approved for beta thalassemia.
FDA approves first CRISPR gene editing treatment that may cure sickle cell disease
Regulators have approved two new gene therapies for sickle cell disease that could potentially cure the inherited blood disorder.
The treatments are the first to be approved based on CRISPR, the gene editing tool that won its inventors the Nobel Prize in 2020.
FDA approves CRISPR-based therapy for sickle cell disease
The FDA has approved the first therapy using CRISPR gene-editing technology to treat sickle cell disease.
The technology has the potential to be applied to other blood disorders, certain cancers, and infectious diseases.
Breakthrough Gene Treatments For Sickle Cell Disease Approved
Regulators have approved two new gene therapies for sickle cell disease, offering hope for a cure for the painful blood disorder
The treatments are designed for patients 12 and older with severe forms of the disease, and one of them is the first therapy based on CRISPR gene editing
Possible Therapy for Sickle Cell Won't Cure Its Racist Legacy - Non Profit News | Nonprofit Quarterly
The FDA is reviewing an experimental gene therapy treatment for sickle cell disease.
Racism has significantly affected the healthcare and outcomes of sickle cell disease patients.