#gene therapy

#gene therapy

Pioneering gene therapy restores sight in young children with a rare genetic condition.

Roatan is attracting ultra-wealthy individuals seeking experimental gene therapies due to its lack of regulations around such treatments.

Gene therapy has significantly improved the vision of toddlers born with severe childhood blindness, providing life-changing outcomes.

Doctors in London have pioneered gene therapy to cure childhood blindness caused by a genetic condition, marking a significant advancement in medical science.

Researchers have identified new mechanisms in Dravet syndrome that highlight novel therapeutic targets, particularly in intronic regions of the SCN1A gene.

Lyfgenia gene therapy successfully cured sickle cell disease in a New Yorker, showcasing a major medical breakthrough.