Northern Minnesota boy is first American to receive groundbreaking treatment for muscular dystrophyColton Belluzzo received groundbreaking gene therapy for Duchenne muscular dystrophy, showing promise in slowing disease progression.
Patient dies following muscular dystrophy gene therapy, Sarepta reportsA patient died from acute liver injury while using Sarepta's Elevidys gene therapy for muscular dystrophy, causing a major stock market reaction.
Young Patient Dies After Receiving Pfizer Gene TherapyThe tragic death of a young boy during a Pfizer medical trial for Duchenne muscular dystrophy has raised concerns and questions among scientists and parents.
Minneapolis parents share journey of having two sons with rare muscle-wasting disorderThe Kasner family faces Duchenne muscular dystrophy with resilience and a strong support network, embracing love and life despite the challenges.
Northern Minnesota boy is first American to receive groundbreaking treatment for muscular dystrophyColton Belluzzo received groundbreaking gene therapy for Duchenne muscular dystrophy, showing promise in slowing disease progression.
Patient dies following muscular dystrophy gene therapy, Sarepta reportsA patient died from acute liver injury while using Sarepta's Elevidys gene therapy for muscular dystrophy, causing a major stock market reaction.
Young Patient Dies After Receiving Pfizer Gene TherapyThe tragic death of a young boy during a Pfizer medical trial for Duchenne muscular dystrophy has raised concerns and questions among scientists and parents.
Minneapolis parents share journey of having two sons with rare muscle-wasting disorderThe Kasner family faces Duchenne muscular dystrophy with resilience and a strong support network, embracing love and life despite the challenges.
Doctors Said These Women's Mutated Genes Wouldn't Harm ThemGenetic screening during IVF can lead to difficult choices regarding embryo selection and raises questions on medical understanding of X-linked diseases.
Transcriptional adaptation upregulates utrophin in Duchenne muscular dystrophy - NatureUtrophin upregulation serves as a compensatory mechanism in DMD, linked to a newly identified process called transcriptional adaptation.
Doctors Said These Women's Mutated Genes Wouldn't Harm ThemGenetic screening during IVF can lead to difficult choices regarding embryo selection and raises questions on medical understanding of X-linked diseases.
Transcriptional adaptation upregulates utrophin in Duchenne muscular dystrophy - NatureUtrophin upregulation serves as a compensatory mechanism in DMD, linked to a newly identified process called transcriptional adaptation.
Meet the branch manager of Berkeley's doggy stick-and-ball libraryPhilip Weiss demonstrated tremendous resilience and innovation despite living with Duchenne muscular dystrophy.He co-founded a company aimed at enhancing life for individuals with disabilities.
Twin boys living with muscle-wasting disease given hope after invitation to clinical trial in USTwins George and Isaac Naughton are seeking help to travel to the US for treatment of Duchenne Muscular Dystrophy.
Native DGC structure rationalizes muscular dystrophy-causing mutationsDystrophin is crucial for muscle cell stability and has significant implications for understanding and treating muscular dystrophies.
The Story Behind Netflix's Moving Documentary The Remarkable Life of IbelinMats Steen's online community provided unexpected support and connection, showcasing the profound impact of virtual friendships in his life.
I am valued here': the extraordinary film that recreates a disabled boy's rich digital lifeMats Steen's story illustrates how gaming can foster meaningful relationships, even amid real-life challenges and isolation.
The Story Behind Netflix's Moving Documentary The Remarkable Life of IbelinMats Steen's online community provided unexpected support and connection, showcasing the profound impact of virtual friendships in his life.
I am valued here': the extraordinary film that recreates a disabled boy's rich digital lifeMats Steen's story illustrates how gaming can foster meaningful relationships, even amid real-life challenges and isolation.