#CRISPR

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gene-editing
LGBTQ Nation
1 week ago
OMG science

Controversial scientist says he'll use gene editing to end HIV & Alzheimer's

Controversial Chinese scientist He Jiankui faces consequences for gene-editing experiments on twins.
Despite criticism, He now aims to use 'base editing' to prevent Alzheimer's disease, setting the stage for potential breakthroughs in curing other diseases. [ more ]
time.com
2 weeks ago
Medicine

Mike Curtis

eGenesis is using CRISPR to edit pig genes for safer human organ transplants. [ more ]
Mail Online
2 weeks ago
OMG science

New AI can CHANGE human genes to cure even the rarest of diseases

AI-designed gene editing system OpenCRISPR-1 reduces off-target editing by 95%, offering potential for precise genetic disease cures. [ more ]
Futurism
3 weeks ago
Artificial intelligence

Startup Uses AI to Edit Human DNA

Profluent uses AI to edit human DNA, creating potential groundbreaking gene editors for disease cures. [ more ]
Engadget
6 months ago
Health

Researchers developed a gene-editing technology that reduces 'bad' cholesterol

A gene-editing treatment called VERVE-101 showed promising results in reducing cholesterol levels in patients with hereditary conditions.
The treatment used CRISPR editing techniques to turn off a cholesterol-raising gene in the liver, resulting in lower levels of LDL-C.
While the therapy has the potential to disrupt current high cholesterol treatments, further studies and FDA approval are needed before it can be widely available. [ more ]
moregene-editing
Nature
1 week ago
Medicine

CRISPR therapy restores some vision to people with blindness

CRISPR-based gene therapy improved vision in individuals with inherited blindness. [ more ]
time.com
4 months ago
Medicine

Here Are the New Drugs and Treatments We Could See in 2024

2023 was a strong year for innovative new drugs, but 2024 is also shaping up to be a milestone year for some exciting therapies.
Eli Lilly could debut a new treatment for Alzheimer's disease that targets amyloid, the protein that builds up in the brains of patients. [ more ]
time.com
5 months ago
Medicine

FDA Approves First CRISPR Treatment in U.S.

The U.S. FDA has approved the first gene therapy treatment based on CRISPR technology.
The treatment, called exa-cel, is approved for sickle cell disease and may also be approved for beta thalassemia. [ more ]
www.mercurynews.com
5 months ago
Medicine

FDA approves first CRISPR gene editing treatment that may cure sickle cell disease

Regulators have approved two new gene therapies for sickle cell disease that could potentially cure the inherited blood disorder.
The treatments are the first to be approved based on CRISPR, the gene editing tool that won its inventors the Nobel Prize in 2020. [ more ]
HuffPost
5 months ago
Medicine

Breakthrough Gene Treatments For Sickle Cell Disease Approved

Regulators have approved two new gene therapies for sickle cell disease, offering hope for a cure for the painful blood disorder
The treatments are designed for patients 12 and older with severe forms of the disease, and one of them is the first therapy based on CRISPR gene editing [ more ]
The Atlantic
5 months ago
Medicine

The CRISPR Era Is Here

Gene-editing technology CRISPR has successfully treated a patient with sickle-cell disease, providing hope for future treatments.
The treatment resulted in the patient living virtually symptom-free, with 29 out of 30 eligible patients experiencing zero pain crises after treatment. [ more ]
www.scientificamerican.com
2 weeks ago
OMG science

Rat Neurons Repair Mouse Brains That Lack a Sense of Smell

Chimeras in the form of mice with rat neurons exhibit brain adaptability for potential disease study and tissue transplantation. [ more ]
www.nytimes.com
3 weeks ago
Artificial intelligence

Generative A.I. Arrives in the Gene Editing World of CRISPR

Generative A.I. technology can create blueprints for microscopic biological mechanisms to edit DNA for battling illnesses with precision and speed. [ more ]
Chicago Tribune
4 months ago
Chicago

Revolutionary gene therapy may offer new life for patients battling chronic sickle cell disease

Gene therapy using CRISPR/Cas9 has been approved by federal regulators as a potential treatment for sickle cell disease.
The University of Chicago Medicine and the University of Illinois at Chicago are among the first medical centers to offer this groundbreaking therapy. [ more ]
www.scientificamerican.com
5 months ago
Science

People with Sickle Cell Deserve More Respect from Health Care Providers

The recent approval of gene-editing treatments for sickle cell disease provides hope for relief from pain and reduced lifespan.
Access to these high-tech treatments remains uncertain and marginalized communities must continue to be supported in their healthcare. [ more ]
KQED
5 months ago
Science

'It's Transformed My Life': FDA Approves First Gene-Editing Treatment for Illness | KQED

The CRISPR treatment for sickle cell disease involves editing a gene with CRISPR and infusing the modified cells back into patients.
The therapy, Casgevy, is designed to be a one-time treatment that alleviates symptoms for a lifetime. [ more ]
www.fastcompany.com
5 months ago
Health

The U.K. approved its first CRISPR gene-editing drugand the U.S. is expected to follow

U.K. regulators have approved the first-ever CRISPR gene-editing drug for the treatment of sickle cell disease and beta thalassemia.
The therapy has shown success in clinical trials and is expected to reach the U.S. by the end of the year.
The gene editing treatment modifies stem cells to boost the production of functional hemoglobin, providing a fix at the DNA level. [ more ]
www.nytimes.com
6 months ago
Health

Sickle-Cell Treatment Created With Gene Editing Wins U.K. Approval

Regulators in Britain have approved the first treatment derived from CRISPR, called Casgevy, for sickle-cell disease and beta thalassemia.
About 2,000 patients in Britain are expected to be eligible for Casgevy treatment.
The FDA is expected to approve Casgevy for sickle-cell patients in the US in early December. [ more ]
BBC News
6 months ago
Health

Casgevy: UK approves gene-editing drug for blood disorders

The UK has approved a gene therapy using the Crispr gene-editing tool to treat sickle cell disease and beta thalassemia, a first in the world.
The treatment involves removing stem cells from a patient's bone marrow and using Crispr to disable the faulty gene, allowing the body to produce functioning haemoglobin.
Trials have shown promising results, with the majority of patients experiencing relief from symptoms and no longer needing blood transfusions. [ more ]
Ars Technica
6 months ago
Health

Crispr gene editing shown to permanently lower high cholesterol

Researchers have shown that a single infusion of a novel gene-editing treatment can reduce cholesterol in a small test on people.
The gene-editing treatment aims to permanently lower cholesterol by using Crispr to edit a gene in the liver.
Preliminary results of the experiment were presented at the American Heart Association's annual meeting. [ more ]
Inverse
6 months ago
Medicine

A CRISPR Gene Therapy Was Just Approved In The UK - That's a Really Big Deal For Medicine

The UK has approved Casgevy, the world's first gene-editing therapy for sickle cell anemia and beta thalassemia.
Casgevy uses CRISPR, a gene editing tool, to correct the mutated hemoglobin gene and produce functional hemoglobin. [ more ]
time.com
6 months ago
Medicine

CRISPR Therapy Gets U.K. Approval, the First in the World

Britain's medicines regulator has approved the world's first gene therapy for sickle cell disease, offering hope to thousands of patients.
Casgevy is the first treatment licensed using the gene editing tool CRISPR, and it targets the problematic gene in a patient's bone marrow stem cells.
Both sickle cell disease and thalassemia are caused by genetic mutations that affect the production of hemoglobin in red blood cells. [ more ]
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