Controversial scientist says he'll use gene editing to end HIV & Alzheimer's
Controversial Chinese scientist He Jiankui faces consequences for gene-editing experiments on twins.
Despite criticism, He now aims to use 'base editing' to prevent Alzheimer's disease, setting the stage for potential breakthroughs in curing other diseases. [ more ]
Researchers developed a gene-editing technology that reduces 'bad' cholesterol
A gene-editing treatment called VERVE-101 showed promising results in reducing cholesterol levels in patients with hereditary conditions.
The treatment used CRISPR editing techniques to turn off a cholesterol-raising gene in the liver, resulting in lower levels of LDL-C.
While the therapy has the potential to disrupt current high cholesterol treatments, further studies and FDA approval are needed before it can be widely available. [ more ]
Generative A.I. Arrives in the Gene Editing World of CRISPR
Generative A.I. technology can create blueprints for microscopic biological mechanisms to edit DNA for battling illnesses with precision and speed. [ more ]
Revolutionary gene therapy may offer new life for patients battling chronic sickle cell disease
Gene therapy using CRISPR/Cas9 has been approved by federal regulators as a potential treatment for sickle cell disease.
The University of Chicago Medicine and the University of Illinois at Chicago are among the first medical centers to offer this groundbreaking therapy. [ more ]
Breakthrough Gene Treatments For Sickle Cell Disease Approved
Regulators have approved two new gene therapies for sickle cell disease, offering hope for a cure for the painful blood disorder
The treatments are designed for patients 12 and older with severe forms of the disease, and one of them is the first therapy based on CRISPR gene editing [ more ]
Gene-editing technology CRISPR has successfully treated a patient with sickle-cell disease, providing hope for future treatments.
The treatment resulted in the patient living virtually symptom-free, with 29 out of 30 eligible patients experiencing zero pain crises after treatment. [ more ]
Casgevy: UK approves gene-editing drug for blood disorders
The UK has approved a gene therapy using the Crispr gene-editing tool to treat sickle cell disease and beta thalassemia, a first in the world.
The treatment involves removing stem cells from a patient's bone marrow and using Crispr to disable the faulty gene, allowing the body to produce functioning haemoglobin.
Trials have shown promising results, with the majority of patients experiencing relief from symptoms and no longer needing blood transfusions. [ more ]