Child with ultra-rare disease gets a treatment just for her
Briefly

The 9-year-old girl's quality of life has significantly improved after receiving a bespoke experimental therapy, which underscores the potential of personalized medicine in treating complex neurological disorders.
This case highlights how tailored therapies can address not just the physical symptoms of neurological disorders but also enhance overall life quality, which can often be overlooked in standard treatments.
Read at Nature
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