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www.theguardian.com
1 month ago
Medicine

Argentinian couple moves to US to allow their toddler to join gene therapy trial

Parents refused to give up despite rare disease diagnosis, traveled for gene therapy trial, showing hope and perseverance. [ more ]
Ars Technica
2 months ago
Health

Lifesaving gene therapy for kids is world's priciest drug at $4.25M

Gene therapy approved for rare disease dramatically improves quality of life for children.
High price of the therapy raises concerns about affordability and access. [ more ]
www.theguardian.com
1 month ago
Medicine

Argentinian couple moves to US to allow their toddler to join gene therapy trial

Parents refused to give up despite rare disease diagnosis, traveled for gene therapy trial, showing hope and perseverance. [ more ]
Ars Technica
2 months ago
Health

Lifesaving gene therapy for kids is world's priciest drug at $4.25M

Gene therapy approved for rare disease dramatically improves quality of life for children.
High price of the therapy raises concerns about affordability and access. [ more ]
moregene-therapy
Alvinalexander
3 months ago
Health

Allergic angina (Kounis Syndrome) in mast cell disease patients

MCAS is a rare disease with only a few cases in certain states like Colorado.
Some doctors may not be familiar with uncommon conditions like mast cell activation disease. [ more ]
www.theguardian.com
2 days ago
Writing

When our young son died, we decided to build him a boat

The story highlights the impact of a rare disease on a child's life and the power of imagination and adventure in coping with challenges. [ more ]
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