#gene-therapies

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#sickle-cell-disease

Innovative Thinking Could Make New Sickle Cell Treatments More Accessible

Gene therapies for sickle cell disease offer hope for functional cure, but high costs and accessibility challenges remain.

FDA approves first CRISPR therapy-here's how it works against sickle cell

The FDA has approved two gene therapies for the treatment of sickle cell disease, one of which is the first CRISPR/Cas9-based treatment to be approved in the US.
Sickle cell disease affects around 100,000 people in the US and can lead to anemia, organ damage, and early death.

Innovative Thinking Could Make New Sickle Cell Treatments More Accessible

Gene therapies for sickle cell disease offer hope for functional cure, but high costs and accessibility challenges remain.

FDA approves first CRISPR therapy-here's how it works against sickle cell

The FDA has approved two gene therapies for the treatment of sickle cell disease, one of which is the first CRISPR/Cas9-based treatment to be approved in the US.
Sickle cell disease affects around 100,000 people in the US and can lead to anemia, organ damage, and early death.
moresickle-cell-disease

Promising new gene therapies for sickle cell are out of reach in countries where they're needed most

Access to gene therapies for sickle cell disease is limited in developing countries like India and Africa.
High prices and complex requirements make gene therapies inaccessible to most patients in these regions.
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